Wilkinson AC, Morita M, Nakauchi H, Yamazaki S.

Branched-chain amino acid depletion conditions bone marrow for hematopoietic stem cell transplantation avoiding amino acid imbalance-associated toxicity.

Exp Hematol. 2018;63:12-16.e1. 

Ir

Barcelos I, Shadiack E, Ganetzky RD, Falk MJ.

Mitochondrial medicine therapies: rationale, evidence, and dosing guidelines.

Curr Opin Pediatr. 2020;32:707-718. 

Ir

Stanescu S, Belanger-Quintana A, Fernandez-Felix BM, Arrieta F, Quintero V, Maldonado MS, Alcaide P, Martínez-Pardo M.

Severe anemia in patients with Propionic acidemia is associated with branched-chain amino acid imbalance.

Orphanet J Rare Dis. 2021;16:226. 

Ir